Intractable Rare Dis Res. 2015;4(2):111-112. (DOI: 10.5582/irdr.2015.01003)
Can Hutchinson-Gilford progeria syndrome be cured in the future?
Rehman NA, Rehman AA, Ashraf IN, Ahmed S
Progeria is a rare genetic disease that manifests with progressive symptoms eventually leading to death. The only current treatment protocol of such patients is symptom based. However, recent trials are testing potential and promising drugs to treat the underlying genetic mutation and increase life expectancy of such patients.